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Best treatments for cystic fibrosis

7 products may treat cystic fibrosis, spanning FDA drug classes such as recombinant human deoxyribonuclease 1, antidote, antidote for acetaminophen overdose. The current highest-rated option is midamor. Ranked below by our independent recall-safety rating (rated where FDA data exists) — not medical advice; always consult a professional.

Quick answer: Of the 7 drugs we list for cystic fibrosis, 3 are available as lower-cost generics, spanning classes such as recombinant human deoxyribonuclease 1, antidote, antidote for acetaminophen overdose. They’re ranked by each drug’s FDA recall-safety record — not clinical effectiveness for cystic fibrosis — so confirm the right choice with your prescriber.

Rated against independent regulatory sources·Last updated August 20, 2026·How we rate

Top-rated picks for cystic fibrosis: 1. Midamor · 2. Pulmozyme · 3. Acetadote

Top-rated treatments for cystic fibrosis, ranked by pharmaranks score
#DrugRatingPharmacy pays
170/100$6View →
270/100View →
3Not yet rated$1View →
4Not yet rated$6View →
5Not yet ratedView →
6Not yet ratedView →
7Not yet ratedView →

Full ranking · 7 treatments

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midamor

Boxed warning

PrescriptionFDA-sourced

70/100

Midamor (Amiloride Hydrochloride) is a medication used to treat Ascites, Cystic Fibrosis, Edema, Heart Failure.

(3 data points)
ascitescystic fibrosisedema

Pharmacy pays

~$6.00 /30

View details →

pulmozyme

PrescriptionFDA-sourced

70/100

Pulmozyme (Dornase Alfa) is a recombinant human deoxyribonuclease 1 used to treat Bronchitis, Cystic Fibrosis.

(5 data points)
recombinant human deoxyribonuclease 1bronchitiscystic fibrosis

Price varies

View details →

acetadote

PrescriptionFDA-sourced

New

Acetadote (Acetylcysteine) is an antidote used to treat Amyloidosis, Bronchiectasis, Bronchitis, Cystic Fibrosis.

antidoteantidote for acetaminophen overdosemucolytic

Pharmacy pays

From ~$0.97· 2 forms Save up to 38% in class
View details →

amiloride hydrochloride

PrescriptionFDA-sourced

New

Amiloride Hydrochloride is a medication used to treat Ascites, Cystic Fibrosis, Edema, Heart Failure.

ascitescystic fibrosisedema

Pharmacy pays

~$6.00 /30

View details →

kalydeco

PrescriptionFDA-sourced

New

Kalydeco (Ivacaftor) is a cystic fibrosis transmembrane conductance regulator potentiator used to treat Cystic Fibrosis.

cystic fibrosis transmembrane conductance regulator potentiatorcystic fibrosis

Price varies

View details →

olpruva

PrescriptionFDA-sourced

New

Olpruva (Sodium Phenylbutyrate) is a nitrogen binding agent used to treat Sickle Cell Anemia, Cystic Fibrosis, Myeloproliferative Disorders, Beta-Thalassemia.

nitrogen binding agentanemia, sickle cellcystic fibrosis

Price varies

View details →

Frequently asked

What treats cystic fibrosis?
Our catalog lists 7 products that may treat cystic fibrosis, based on NIH RxClass (MED-RT “may treat”) drug-classification data — not the verbatim FDA label. They're rated where FDA recall-safety data exists; the current top-rated option is midamor.
What is the best-rated treatment for cystic fibrosis?
By our independent recall-safety rating — not an efficacy measure — midamor ranks highest among the products we list for cystic fibrosis. Always consult a professional.
How are these treatments ranked?
By our independent score, currently based on FDA regulatory recall-safety data (the methodology blends additional sources as they come online). See the How we rate page.
What types of drugs treat cystic fibrosis?
Treatments for cystic fibrosis span FDA drug classes including recombinant human deoxyribonuclease 1, antidote, antidote for acetaminophen overdose, mucolytic, cystic fibrosis transmembrane conductance regulator potentiator. Compare every option side by side, ranked by independent rating, above.

Treatment associations are derived from NIH RxClass (MED-RT “may treat”) drug-classification data — not the verbatim FDA label. This is general reference, not medical advice — always consult a licensed professional.